A new gene therapy for Dravet syndrome from @EncodedTx increases life expectancy and limits seizures in mice. It was also well-tolerated in monkeys, which @UrnovFyodor calls "tremendous news." My latest for @Spectrum:
spectrumnews.org/news/gene-t…
Special thanks to @EncodedTx for helping to develop this exciting series with @curedravet. This first session is an excellent introduction to #AAV-mediated #genetherapy by Dr. Michael Lawlor