๐๐๐ ๐ ๐๐ง๐ ๐ญ๐ก๐๐ซ๐๐ฉ๐ฒ ๐ฆ๐ข๐ฅ๐๐ฌ๐ญ๐จ๐ง๐ ๐ข๐ง ๐๐ฎ๐ซ๐จ๐ฉ๐. ๐๐จ๐ซ๐ฐ๐๐ฒ issued a reimbursement recommendation for ๐๐๐๐๐๐๐๐. ๐
๐จ๐ฅ๐ฅ๐จ๐ฐ ๐๐๐๐ค๐๐๐ง๐ ๐จ๐ง ๐๐ข๐ง๐ค๐๐๐ข๐ง lnkd.in/e5GY5tAR & ๐๐ฎ๐๐ฌ๐๐ซ๐ข๐๐ ๐ญ๐จ ๐๐ฎ๐ซ ๐๐๐ฐ๐ฌ๐ฅ๐๐ญ๐ญ๐๐ซ.
๐ Meet PackGene at #BSGCT2025 in London!
๐๏ธJune 20
๐Royal Holloway University
Letโs talk AAV, LVV, mRNA, & plasmid innovation with Xisha Huang.
#GeneTherapy #Biotech #CDMO #PackGene
Weโre heading to #EACR2025 in Lisbon!
๐Booth #17ย
๐๏ธย June 16โ19
Explore our full-service #CRO and #CDMO offerings:
๐งฌย AAV | Lentivirus | Plasmid | mRNA & LNP
Letโs talk cancer gene therapy innovation.
๐ฉย [email protected]
#GeneTherapy #CancerResearch #Biotech #PackGene
Weโre at #NVGCT2025 โ๏ธJune 10โ11 in Lenteren, Netherland!
Stop by the PackGene booth & meet Dr. Heng Hu to learn about our AAV, LVV, mRNA & plasmid platforms.
packgene.com/event/nvgct-annโฆ
#GeneTherapy #Biotech #mRNA #AAV #PackGene
PackGene Biotech retweeted
Conquering the Complexities of AAV Manufacturing: Advances in Efficiency, Scalability, Compliance
GEN talked with several CDMOs and/or CROs about new ways they are addressing AAV manufacturing challenges.
@PackGeneBiotech @CRiverLabs @LonzaGroup #AAV
hubs.li/Q03prQ2j0
๐จย PackGene is heading to #AACR2025!
๐ฏย Visit us at Booth 4346ย in Chicago, Apr 25โ30
๐งฌย Discover how our AAV, lentiviral, and mRNA platforms are accelerating cancer research.
๐ย Stop by for a chat, insights, and free swag!
๐ย Academic promo: packgene.com/promotion/acadeโฆ
#GeneTherapy
24-month data from Beacon Therapeutics' AGTC-501 HORIZON Trial for XLRP now in @AmerAcadOphth! Promising results in gene therapy.
#GeneTherapy #RetinalDisease #XLRP #AAV #Packgene
packgene.com/frontier/250319โฆ
Arbor Biotechnologies closes $73.9M Series C to advance ABO-101 for Primary Hyperoxaluria Type 1 (PH1). This milestone highlights the potential of CRISPR Cas12i2 and signals continued investor confidence in groundbreaking therapies.
#GeneEditing #CRISPR
packgene.com/frontier/250319โฆ
HUGE NEWS! Beam Therapeutics achieves FIRST-EVER clinical genetic correction in AATD trial!
ย BEAM-302 shows:
โ
โฌ๏ธย AAT levels (exceeding therapeutic threshold!)
โ
โฌ๏ธย 78% reduction in mutant Z-AAT!
โ
ย Corrected M-AAT production!
โ
ย Great safety profile!
investors.beamtx.com/news-reโฆ
Academic Discovery Engine
Accelerate your research from design to delivery with academic-exclusive offers
packgene.com/support/promotiโฆ
#AAV #ViralVector #CRISPR #ResearchOptimization
๐งฌThis #RareDiseaseDay, weโre breaking barriers in gene therapy!
โ
Advancing SPG56 & OTOF hearing loss treatments
๐No patient left behind. Learn more: packgene.com/event/rare-diseโฆ
#GeneTherapy #RareDiseases #BreakingBarriers #PackGene
Allogene ($ALLO) gets FDA IND clearance for ALLO-329, an allogeneic CAR T for autoimmune diseases.
Phase1 trial starts mid-2025 for lupus, myopathies, & systemic sclerosis. Targets CD19+ B cells & CD70+ T cells. Daggerยฎ tech may eliminate lymphodepletion.
packgene.com/frontier/250131โฆ
ELEVIDYS shows sustained benefits for 2 YEARS in ambulatory #DMD patients! Sarepta's EMBARK study delivers promising long-term data. โจ
packgene.com/frontier/250131โฆ
#RareDisease #GeneTherapy #AAV #Packgene #Sarepta
Weโre at #PMWC2025! Visit PackGene at Booth A421 to discuss our GMP viral (AAV)ย and non-viral solutions. Letโs innovate together and shape the future of precision medicine.
Booth A421โsee you there!
#GeneTherapy #AAV #PrecisionMedicine #Biotech
Vertex & Orna team up to develop gene therapies for SCD & TDT! $65M upfront to boost RNA-based innovations using Orna's LNP tech. This collab drives progress toward better rare disease treatments.
packgene.com/frontier/250110โฆ
#GeneTherapy #SCD #VertexPharma
A Global Alliance to Save Lives: How Two Parents and PackGene Are Redefining Whatโs Possible in Gene Therapy with Help from Weill Cornell Medicine
Read more๐packgene.com/news/250107/
Video link: youtube.com/watch?v=QwlYjWxEโฆ
#GeneTherapy
Novartis' OAV101 IT gene therapy shows promise for type II SMA patients aged 2-17! ๐Favorable Phase III results could expand options for older pediatric patients.
packgene.com/frontier/250109โฆ
#GeneTherapy #SMA #RareDisease
โจMedical Breakthroughs of 2024โจ
ยท Enhertu & Tagrisso redefine cancer care
ยท GLP-1 meds tackle obesity, heart disease, & sleep apnea
ยท Lenacapavir: 100% HIV prevention
ยท New treatments for Duchenne MD, schizophrenia & more
packgene.com/frontier/202501โฆ
#GeneTherapy
GEMMABio raises $34M to advance #GeneTherapy for rare diseases! With strong partnerships and innovative approaches, theyโre redefining treatment accessibility.
packgene.com/frontier/241227โฆ
#HealthcareInnovation #RareDiseases












