A global network of non-profit organisations supporting families affected by Niemann Pick Diseases
Joined March 2014
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Chris Andrews, Father to Abby and Belle, two children with Niemann-Pick disease type C, shares his story with those in attendance at last month's Niemann-Pick Type C Disease Patient-Focused Drug Development Meeting.
To learn more... youtube.com/watch?v=Gfh8A7Rt…
We need YOUR help! ❤️
Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance... surveymonkey.com/r/orphazyme…
We need YOUR help! ❤️
Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance Orphazyme is investigating is called arimoclomol citrate, which is... surveymonkey.com/r/orphazyme…
We need YOUR help! ❤️
Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance Orphazyme is investigating is called arimoclomol citrate, which is... surveymonkey.com/r/orphazyme…
We need YOUR help! ❤️
Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance Orphazyme is investigating is called arimoclomol citrate, which is... surveymonkey.com/r/orphazyme…
“NNPDF Industry Update Webinar Series featuring Intrabio”
INPDA International Niemann-Pick Disease Alliance member group the National Niemann-Pick Disease Foundation, Inc.'s Industry Update Webinar Series will continue on the... nnpdf.org/news-media/nnpdf-w…
In the following video Helenida Tauil reports from the Associação Niemann-Pick Brasil's 1st Symposium on Rare Diseases in Londrina
For further information on INPDA International Niemann-Pick Disease Alliance member group ANPB,... youtube.com/watch?v=2cDqbYOU…
Less than SIX months to go until INPDA founding member group Niemann-Pick UK's Annual Family Conference & Interactive Workshop on Niemann-Pick Disease(s)! facebook.com/inpda.org/posts…
Niemann-Pick Type C Externally-led Patient-Focused Drug Development Meeting (video stream now available!)
The Niemann-Pick Type C (NPC) externally led Patient-Focused Drug Development (PFDD) meeting is a groundbreaking initiative... youtube.com/watch?v=iHcDkdrU…
INPDA International Niemann-Pick Disease Alliance Secretary, and Niemann-Pick UK Chief Executive Toni Mathieson was honoured to be in attendance at the Niemann-Pick Type C Patient-Focused Drug Development in... facebook.com/inpda.org/posts…
