AgilisBio retweeted
Agilis team Working hard to help these families! #CureAADC
AgilisBio retweeted
$PTCT to Acquire Agilis Biotherapeutics for $50M cash + $150M stock
Everyone getting into gene therapy...
AgilisBio retweeted
Nabbing late-stage drug, PTC acquires gene therapy startup Agilis for $200M in cash/stock
$PTCT +8%
@BrittanyMeiling
endpts.com/nabbing-late-stag…
AgilisBio retweeted
Delighted to spend a day talking about AADC Deficiency with Dr Hwu and NIH, at NCATS #NCATS #NIH #genetherapy #cureAADC
AgilisBio retweeted
Blessed to have known Charles Krauthammer. He is a brilliant, kind, elegant, funny and perhaps above all, wise, man. An intellectual giant whose voice will be missed beyond measure.
AgilisBio retweeted
An abstract regarding @AgilisBio's principal investigator, AGIL-AADC, a #genetherapy, and its clinical trials for AADC deficiency was presented at the American Society of Gene and Cell Therapy (ASGCT) in Chicago.
READ: raredr.com/link/3465
AgilisBio retweeted
Katherine High @spark_tx gave a great round off to her plenary session, #genetherapy coming of age #ASGCT18
AgilisBio retweeted
We want to see you show off your muscles in your new Lend Us Some Muscle t-shirts 👚👕 or tattoos in honor of Friedreich's Ataxia Awareness Day [May 19] 💪. Or show us your muscl-y-est pose. Tag and share your pics 📸! Don’t forget to hashtag #LendUsSomMuscle #LUSM2018 #CureFA
AgilisBio retweeted
NCATS and NIH talk about partnerships with rare disease researchers. Seems like a great resource. Good work to @SangamoTx and @AgilisBio for taking advantage. @ncats_nih_gov #WODCUSA #RareDisease
AgilisBio retweeted
Replying to @NIH
@NIH initiatives on gene editing, with great resource #raredisease #clinical #research network and collaboration with @AgilisBio to develop gene therapy for #patients good effort done on coordinating, disseminating and educating! @OrphanConf #WODCUSA @AtaxiaUK – at Fort Washington, MD
AgilisBio retweeted
Breaking News! The ASF’s sixth multi-disciplinary Angelman Syndrome Clinic will open on May 7th at NYU Langone Health in New York, NY! Made possible by generous donors, the new NYU AS Clinic was created through a partnership between the ASF and @nyulangone.
AgilisBio retweeted
FA researcher Professor Arnulf Koeppen, MD receives 2018 Dr. L. Clarke Jr. and Elaine F. Stout Award for his work in understanding FA neuropathology". #CureFA @TheUSCAP @AlbanyMed #USCAP2018
AgilisBio retweeted
Your FAST board and FIRE team are working hard to find a cure for Angelman syndrome. #angelmansyndrome #myreason — at Texas A&M University facebook.com/cureangelman.or…
AgilisBio retweeted
Had lots of fun at the Prestigious DeVere Selsdon Estate today! Yay they’ve nominated us as their chosen Charity to Partner with thanks to Caroline Morrone, Tracey Montgomery and Matt Brierley.
Had a chance... facebook.com/AADCResearchTru…
AgilisBio retweeted
Today kicks off a virtual event for #RareDiseaseDay from the @US_FDA featuring an announcement regarding a #NORD/FDA collaboration & video interviews including one from NORD's Director of Research Programs, Vanessa Boulanger: bit.ly/2EWKbHO
AgilisBio retweeted
TOMORROW is #RareDiseaseDay! Retweet to raise awareness! What are you doing for the big day tomorrow?
AgilisBio retweeted
🚨 We’re LIVE!! 🚨 Can’t think of a better way to start the week. The Ataxian is available NOW on iTunes, Amazon, Google Play, Xbox, and Sony Playstation Network. 👏👏👏 📝 Show us some ❤️ with a review! #thankyou #CureFA #raredisease #retweet #mustsee vimeo.com/127990377
































